Richard Jude Samulski
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Richard Jude Samulskibiology Degrees
Biology
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Virology
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Molecular Biology
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Biology
Richard Jude Samulski's Degrees
- PhD Biochemistry University of California, Berkeley
- Bachelors Chemistry University of California, Berkeley
Why Is Richard Jude Samulski Influential?
(Suggest an Edit or Addition)Richard Jude Samulski's Published Works
Number of citations in a given year to any of this author's works
Total number of citations to an author for the works they published in a given year. This highlights publication of the most important work(s) by the author
Published Works
- Membrane-Associated Heparan Sulfate Proteoglycan Is a Receptor for Adeno-Associated Virus Type 2 Virions (1998) (1361)
- Production of High-Titer Recombinant Adeno-Associated Virus Vectors in the Absence of Helper Adenovirus (1998) (1287)
- Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield (1999) (1247)
- Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain (1994) (1039)
- Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector (1996) (932)
- Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction with Broad Specificity (2002) (793)
- Adeno-associated virus serotypes: vector toolkit for human gene therapy. (2006) (779)
- Second-strand synthesis is a rate-limiting step for efficient transduction by recombinant adeno-associated virus vectors (1996) (769)
- Helper-free stocks of recombinant adeno-associated viruses: normal integration does not require viral gene expression (1989) (738)
- αVβ5 integrin: a co-receptor for adeno-associated virus type 2 infection (1999) (655)
- Dystrophin immunity in Duchenne's muscular dystrophy. (2010) (550)
- Infectious Entry Pathway of Adeno-Associated Virus and Adeno-Associated Virus Vectors (2000) (530)
- Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo (2003) (526)
- Production and characterization of adeno-associated viral vectors (2006) (484)
- Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector (1996) (465)
- A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication (1987) (451)
- Cloning of adeno-associated virus into pBR322: rescue of intact virus from the recombinant plasmid in human cells. (1982) (422)
- Integration of adeno-associated virus (AAV) and recombinant AAV vectors. (2004) (421)
- Engineering adeno-associated virus vectors for gene therapy (2020) (416)
- Preclinical differences of intravascular AAV9 delivery to neurons and glia: a comparative study of adult mice and nonhuman primates. (2011) (397)
- Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors. (2000) (386)
- Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector. (2012) (346)
- AAV-Mediated Gene Therapy for Research and Therapeutic Purposes. (2014) (344)
- Packaging Capacity of Adeno-Associated Virus Serotypes: Impact of Larger Genomes on Infectivity and Postentry Steps (2005) (325)
- AlphaVbeta5 integrin: a co-receptor for adeno-associated virus type 2 infection. (1999) (304)
- AAV vectors: is clinical success on the horizon? (2000) (301)
- Selective and rapid uptake of adeno-associated virus type 2 in brain. (1998) (301)
- Rescue of adeno-associated virus from recombinant plasmids: Gene correction within the terminal repeats of AAV (1983) (293)
- Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectors. (2011) (277)
- Global CNS Gene Delivery and Evasion of Anti-AAV Neutralizing Antibodies by Intrathecal AAV Administration in Non-Human Primates (2012) (272)
- Remodeling of cortical bone allografts mediated by adherent rAAV-RANKL and VEGF gene therapy (2005) (271)
- The role of Kupffer cell oxidant production in early ethanol-induced liver disease. (2001) (248)
- α2,3 and α2,6 N-Linked Sialic Acids Facilitate Efficient Binding and Transduction by Adeno-Associated Virus Types 1 and 6 (2006) (247)
- Site-specific integration by adeno-associated virus. (1990) (244)
- Adeno-associated virus vectors for gene therapy: more pros than cons? (2000) (244)
- Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'γ)2 antibody (1999) (228)
- Polymeric nanogels produced via inverse microemulsion polymerization as potential gene and antisense delivery agents. (2002) (224)
- Role for highly regulated rep gene expression in adeno-associated virus vector production (1997) (220)
- Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle (2010) (216)
- Single Amino Acid Changes Can Influence Titer, Heparin Binding, and Tissue Tropism in Different Adeno-Associated Virus Serotypes (2006) (210)
- Viral vectors for gene delivery to the central nervous system (2012) (210)
- Regulated high level expression of a human gamma-globin gene introduced into erythroid cells by an adeno-associated virus vector. (1992) (195)
- AAV hybrid serotypes: improved vectors for gene delivery. (2005) (192)
- Cellular recombination pathways and viral terminal repeat hairpin structures are sufficient for adeno-associated virus integration in vivo and in vitro (1997) (185)
- Cross-Dressing the Virion: the Transcapsidation of Adeno-Associated Virus Serotypes Functionally Defines Subgroups (2004) (182)
- Production of Recombinant Adeno-associated Virus Vectors Using Suspension HEK293 Cells and Continuous Harvest of Vector From the Culture Media for GMP FIX and FLT1 Clinical Vector. (2016) (182)
- Titration of AAV-2 particles via a novel capsid ELISA: packaging of genomes can limit production of recombinant AAV-2 (1999) (176)
- Adeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspective. (2015) (176)
- Self-complementary adeno-associated virus serotype 2 vector: global distribution and broad dispersion of AAV-mediated transgene expression in mouse brain. (2003) (175)
- Adeno-associated virus vectorology, manufacturing, and clinical applications. (2012) (173)
- Adeno-associated virus: integration at a specific chromosomal locus. (1993) (173)
- In vitro resolution of covalently joined AAV chromosome ends (1990) (170)
- Alpha2,3 and alpha2,6 N-linked sialic acids facilitate efficient binding and transduction by adeno-associated virus types 1 and 6. (2006) (170)
- Engineering and selection of shuffled AAV genomes: a new strategy for producing targeted biological nanoparticles. (2008) (166)
- Adeno-Associated Virus Type 2 Contains an Integrin α5β1 Binding Domain Essential for Viral Cell Entry (2006) (163)
- Adeno-associated viral vectors as gene delivery vehicles. (2000) (163)
- Parkinson's Disease Gene Therapy: Success by Design Meets Failure by Efficacy (2013) (158)
- A novel 165-base-pair terminal repeat sequence is the sole cis requirement for the adeno-associated virus life cycle (1997) (154)
- Identification of a repeated sequence element required for efficient encapsidation of the adenovirus type 5 chromosome (1987) (154)
- Separate Basic Region Motifs within the Adeno-Associated Virus Capsid Proteins Are Essential for Infectivity and Assembly (2006) (152)
- Enhancement of Adeno-Associated Virus Infection by Mobilizing Capsids into and Out of the Nucleolus (2008) (151)
- Optimization of self-complementary AAV vectors for liver-directed expression results in sustained correction of hemophilia B at low vector dose. (2008) (148)
- Long-term gene transfer in porcine myocardium after coronary infusion of an adeno-associated virus vector. (1996) (148)
- Phenotypic correction of Fanconi anemia in human hematopoietic cells with a recombinant adeno-associated virus vector. (1994) (144)
- Adeno-associated virus as a gene therapy vector: vector development, production and clinical applications. (2005) (142)
- Robust spinal motor neuron transduction following intrathecal delivery of AAV9 in pigs (2011) (142)
- Comparison of adeno-associated viral vector serotypes for spinal cord and motor neuron gene delivery. (2011) (141)
- Biology of adeno-associated viral vectors in the central nervous system (2014) (140)
- Features of the adeno-associated virus origin involved in substrate recognition by the viral Rep protein (1993) (140)
- Insertional mutagenesis of AAV2 capsid and the production of recombinant virus. (1999) (139)
- Delivery of the Cu/Zn-superoxide dismutase gene with adenovirus reduces early alcohol-induced liver injury in rats. (2001) (139)
- Roles of Adeno-Associated Virus Rep Protein and Human Chromosome 19 in Site-Specific Recombination (2000) (138)
- Structural Characterization of the Dual Glycan Binding Adeno-Associated Virus Serotype 6 (2010) (137)
- Directed Evolution of a Novel Adeno-associated Virus (AAV) Vector That Crosses the Seizure-compromised Blood-Brain Barrier (BBB). (2010) (129)
- Host Cell DNA Repair Pathways in Adeno-Associated Viral Genome Processing (2006) (126)
- Recombinant adeno-associated virus-mediated gene transfer into hematopoietic progenitor cells. (1994) (126)
- Cytoplasmic Trafficking, Endosomal Escape, and Perinuclear Accumulation of Adeno-Associated Virus Type 2 Particles Are Facilitated by Microtubule Network (2012) (124)
- Building a better vector: the manipulation of AAV virions. (2000) (122)
- Adeno-associated virus (AAV) gene therapy for neurological disease (2013) (120)
- Autoimmune anemia in macaques following erythropoietin gene therapy. (2004) (119)
- Novel Transcriptional Regulatory Signals in the Adeno-Associated Virus Terminal Repeat A/D Junction Element (2000) (119)
- Sustained and complete phenotype correction of hemophilia B mice following intramuscular injection of AAV1 serotype vectors. (2001) (119)
- Structure and Dynamics of Adeno-Associated Virus Serotype 1 VP1-Unique N-Terminal Domain and Its Role in Capsid Trafficking (2013) (118)
- Persistent expression of canine factor IX in hemophilia B canines (1999) (116)
- Comparative transduction efficiency of AAV vector serotypes 1-6 in the substantia nigra and striatum of the primate brain. (2010) (116)
- Characterization of a recombinant adeno-associated virus type 2 Reference Standard Material. (2010) (113)
- Proteasome inhibitors enhance gene delivery by AAV virus vectors expressing large genomes in hemophilia mouse and dog models: a strategy for broad clinical application. (2010) (112)
- Improved survival and reduced phenotypic severity following AAV9/MECP2 gene transfer to neonatal and juvenile male Mecp2 knockout mice. (2013) (110)
- Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery. (2002) (107)
- Gene delivery of Cu/Zn‐superoxide dismutase improves graft function after transplantation of fatty livers in the rat (2000) (102)
- Adeno-associated virus vectors: potential applications for cancer gene therapy (2005) (100)
- Gene therapy: targeting the myocardium (2007) (99)
- Capsid Antibodies to Different Adeno-Associated Virus Serotypes Bind Common Regions (2013) (97)
- Recombinant adeno-associated virus (rAAV)-mediated expression of a human gamma-globin gene in human progenitor-derived erythroid cells. (1994) (97)
- Adeno-associated virus type 2 contains an integrin alpha5beta1 binding domain essential for viral cell entry. (2006) (96)
- Viral vectors and delivery strategies for CNS gene therapy. (2010) (96)
- Mutagenesis of Adeno-Associated Virus Type 2 Capsid Protein VP1 Uncovers New Roles for Basic Amino Acids in Trafficking and Cell-Specific Transduction (2010) (94)
- Production of Recombinant Adeno‐Associated Viral Vectors (1999) (94)
- Adenovirus E1B 55-Mr polypeptide facilitates timely cytoplasmic accumulation of adeno-associated virus mRNAs (1988) (93)
- Efficient transduction of vascular endothelial cells with recombinant adeno-associated virus serotype 1 and 5 vectors. (2005) (91)
- AAV's anatomy: roadmap for optimizing vectors for translational success. (2010) (89)
- Differential myocardial gene delivery by recombinant serotype-specific adeno-associated viral vectors. (2004) (89)
- Adeno-Associated Virus Type 2 (AAV2) Capsid-Specific Cytotoxic T Lymphocytes Eliminate Only Vector-Transduced Cells Coexpressing the AAV2 Capsid In Vivo (2007) (88)
- Investigation of the cause of death in a gene-therapy trial. (2009) (88)
- Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs (2012) (88)
- Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Associated Virus Clinical Trial (2014) (87)
- Delivery of MDR1 small interfering RNA by self-complementary recombinant adeno-associated virus vector. (2005) (87)
- The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers. (2000) (86)
- Single Amino Acid Modification of Adeno-Associated Virus Capsid Changes Transduction and Humoral Immune Profiles (2012) (86)
- Efficient retrograde neuronal transduction utilizing self-complementary AAV1. (2008) (85)
- Generation of novel AAV variants by directed evolution for improved CFTR delivery to human ciliated airway epithelium. (2009) (83)
- Production of Recombinant Adeno‐Associated Viral Vectors and Use in In Vitro and In Vivo Administration (1999) (83)
- Self-complementary AAV virus (scAAV) safe and long-term gene transfer in the trabecular meshwork of living rats and monkeys. (2010) (82)
- Cu/Zn-superoxide dismutase gene attenuates ischemia-reperfusion injury in the rat kidney. (2001) (82)
- Engineering and Selection of Shuffled AAV Genomes: A New Strategy for Producing Targeted Biological Nanoparticles. (2008) (78)
- Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB). (2010) (78)
- Factors Influencing Adeno-Associated Virus-Mediated Gene Transfer to Human Cystic Fibrosis Airway Epithelial Cells: Comparison with Adenovirus Vectors (1998) (77)
- Existence of transient functional double-stranded DNA intermediates during recombinant AAV transduction (2007) (75)
- Recombinant Adeno-Associated Virus Utilizes Host Cell Nuclear Import Machinery To Enter the Nucleus (2014) (74)
- Adeno-associated Virus as a Mammalian DNA Vector. (2015) (74)
- Adeno-associated virus (AAV) site-specific recombination does not require a Rep-dependent origin of replication within the AAV terminal repeat (2001) (73)
- Overexpression of SOD in retina: need for increase in H2O2-detoxifying enzyme in same cellular compartment. (2011) (73)
- The AAV vector toolkit: poised at the clinical crossroads. (2012) (72)
- Colocalization of adeno-associated virus Rep and capsid proteins in the nuclei of infected cells (1992) (72)
- Marker Rescue of Adeno-Associated Virus (AAV) Capsid Mutants: a Novel Approach for Chimeric AAV Production (2003) (72)
- Comparison of the effect of adenoviral delivery of three superoxide dismutase genes against hepatic ischemia-reperfusion injury. (2001) (72)
- Adeno-Associated Virus (AAV) Versus Immune Response (2019) (72)
- AAV as a viral vector for human gene therapy (1995) (72)
- Engraftment of a Galactose Receptor Footprint onto Adeno-associated Viral Capsids Improves Transduction Efficiency* (2013) (71)
- Cellular immune response to cryptic epitopes during therapeutic gene transfer (2009) (71)
- Optimal design of a single recombinant adeno-associated virus derived from serotypes 1 and 2 to achieve more tightly regulated transgene expression from nonhuman primate muscle. (2004) (70)
- Role of viral vectors and virion shells in cellular gene expression. (2004) (70)
- Delivering Transgenic DNA Exceeding the Carrying Capacity of AAV Vectors. (2016) (69)
- Therapeutic liabilities of in vivo viral vector tropism: adeno-associated virus vectors, NMDAR1 antisense, and focal seizure sensitivity. (2002) (69)
- Biosafety of recombinant adeno-associated virus vectors. (2014) (68)
- Surface-Exposed Adeno-Associated Virus Vp1-NLS Capsid Fusion Protein Rescues Infectivity of Noninfectious Wild-Type Vp2/Vp3 and Vp3-Only Capsids but Not That of Fivefold Pore Mutant Virions (2007) (66)
- Construction of a recombinant human parvovirus B19: adeno-associated virus 2 (AAV) DNA inverted terminal repeats are functional in an AAV-B19 hybrid virus. (1989) (65)
- Adeno‐associated virus serotypes 1 to 5 mediated tumor cell directed gene transfer and improvement of transduction efficiency (2005) (65)
- Sub-2 Å Ewald curvature corrected structure of an AAV2 capsid variant (2018) (64)
- Secretion of extracellular superoxide dismutase from muscle transduced with recombinant adenovirus inhibits the growth of B16 melanomas in mice. (2003) (64)
- Cardiac I-1c overexpression with reengineered AAV improves cardiac function in swine ischemic heart failure. (2014) (63)
- AAV9.I-1c Delivered via Direct Coronary Infusion in a Porcine Model of Heart Failure Improves Contractility and Mitigates Adverse Remodeling (2013) (63)
- Viral receptors and vector purification: New approaches for generating clinical-grade reagents (1999) (62)
- Intraarticular factor IX protein or gene replacement protects against development of hemophilic synovitis in the absence of circulating factor IX. (2008) (62)
- Little vector, big gene transduction: fragmented genome reassembly of adeno-associated virus. (2010) (60)
- Combination therapy utilizing shRNA knockdown and an optimized resistant transgene for rescue of diseases caused by misfolded proteins (2011) (59)
- Self-complementary AAV2.5-BMP2-coated femoral allografts mediated superior bone healing versus live autografts in mice with equivalent biomechanics to unfractured femur. (2011) (58)
- Human Galectin 3 Binding Protein Interacts with Recombinant Adeno-Associated Virus Type 6 (2012) (58)
- Development and Characterization of Novel Empty Adenovirus Capsids and Their Impact on Cellular Gene Expression (2003) (57)
- Effects of Adeno-Associated Virus DNA Hairpin Structure on Recombination (2005) (55)
- Kinetics of Recombinant Adeno-Associated Virus-Mediated Gene Transfer (2000) (55)
- Surface Loop Dynamics in Adeno-Associated Virus Capsid Assembly (2008) (55)
- BAX 335 hemophilia B gene therapy clinical trial results - potential impact of CpG sequences on gene expression. (2020) (55)
- Double-stranded RNA innate immune response activation from long-term adeno-associated virus vector transduction. (2018) (55)
- Adeno-associated virus capsid antigen presentation is dependent on endosomal escape. (2013) (54)
- Adeno-associated virus vectors for therapeutic gene transfer. (2003) (54)
- Ocular gene transfer with self-complementary AAV vectors. (2007) (53)
- Adeno-associated Viral Vectors (1995) (52)
- Adeno-associated virus-mediated gene transfer of the heart/muscle adenine nucleotide translocator (ANT) in mouse (2005) (52)
- Oversized AAV transductifon is mediated via a DNA-PKcs-independent, Rad51C-dependent repair pathway. (2013) (52)
- Production of Recombinant Adeno‐Associated Viral Vectors for In Vitro and In Vivo Use (2007) (50)
- Characterization of a novel adeno-associated viral vector with preferential oligodendrocyte tropism (2015) (49)
- Delivery of Cu/Zn-superoxide dismutase genes with a viral vector minimizes liver injury and improves survival after liver transplantation in the rat. (2000) (49)
- Preclinical safety evaluation of subretinal AAV2.sFlt-1 in non-human primates (2011) (48)
- Mechanistic Insights into the Enhancement of Adeno-Associated Virus Transduction by Proteasome Inhibitors (2013) (48)
- Mechanisms of AAV transduction in glaucoma‐associated human trabecular meshwork cells (2006) (47)
- Optimization of scAAVIL-1ra In Vitro and In Vivo to Deliver High Levels of Therapeutic Protein for Treatment of Osteoarthritis (2013) (47)
- AAV Exploits Subcellular Stress Associated with Inflammation, Endoplasmic Reticulum Expansion, and Misfolded Proteins in Models of Cystic Fibrosis (2011) (46)
- Single-polarity recombinant adeno-associated virus 2 vector-mediated transgene expression in vitro and in vivo: mechanism of transduction. (2008) (44)
- Embryonic substantia nigra grafts in the mesencephalon send neurites to the host striatum in non‐human primate after overexpression of GDNF (2009) (43)
- Gene transfer in human lymphocytes using a vector based on adeno-associated virus. (1992) (43)
- AAV Gene Therapy for MPS1-associated Corneal Blindness (2016) (42)
- Development of Patient-specific AAV Vectors After Neutralizing Antibody Selection for Enhanced Muscle Gene Transfer. (2016) (42)
- Inducible Adeno-Associated Virus-Mediated IL-2 Gene Therapy Prevents Autoimmune Diabetes (2011) (42)
- Single-copy transduction and expression of human gamma-globin in K562 erythroleukemia cells using recombinant adeno-associated virus vectors: the effect of mutations in NF-E2 and GATA-1 binding motifs within the hypersensitivity site 2 enhancer. (1993) (41)
- Supramolecular nanomimetics: replication of micelles, viruses, and other naturally occurring nanoscale objects. (2007) (41)
- Blood-brain barrier shuttle peptides enhance AAV transduction in the brain after systemic administration. (2018) (40)
- Cytotoxic-T-Lymphocyte-Mediated Elimination of Target Cells Transduced with Engineered Adeno-Associated Virus Type 2 Vector In Vivo (2009) (40)
- Optimizing gene delivery vectors for the treatment of heart disease. (2008) (40)
- Viral Single-Strand DNA Induces p53-Dependent Apoptosis in Human Embryonic Stem Cells (2011) (40)
- Self-complementary AAV mediates gene targeting and enhances endonuclease delivery for double-strand break repair (2010) (40)
- Adeno-associated virus of a single-polarity DNA genome is capable of transduction in vivo. (2008) (39)
- Gene Therapy for Human Hemoglobinopathies (1993) (39)
- Direct Interaction of Human Serum Proteins with AAV Virions to Enhance AAV Transduction: Immediate Impact on Clinical Applications (2016) (38)
- Human Neural Stem Cells Survive Long Term in the Midbrain of Dopamine‐Depleted Monkeys After GDNF Overexpression and Project Neurites Toward an Appropriate Target (2014) (38)
- Restoration of cytoskeleton homeostasis after gigaxonin gene transfer for giant axonal neuropathy. (2013) (37)
- Arsenic Trioxide Stabilizes Accumulations of Adeno-Associated Virus Virions at the Perinuclear Region, Increasing Transduction In Vitro and In Vivo (2013) (37)
- Prediction of Adeno-Associated Virus Neutralizing Antibody Activity for Clinical Application (2015) (37)
- The genus Dependovirus (2005) (37)
- An emerging adeno-associated viral vector pipeline for cardiac gene therapy. (2013) (36)
- Ex vivo serotype-specific transduction of equine joint tissue by self-complementary adeno-associated viral vectors. (2009) (36)
- Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism (2016) (36)
- Efficient Retrograde Neuronal Transduction Utilizing Self-complementary AAV1. (2008) (36)
- Chronic ethanol increases adeno‐associated viral transgene expression in rat liver via oxidant and NFκB‐dependent mechanisms (2000) (35)
- Fluorescent viral vectors: A new technique for the pharmacological analysis of gene therapy (1998) (34)
- AAVR: A Multi-Serotype Receptor for AAV. (2016) (34)
- β-Cell–Specific IL-2 Therapy Increases Islet Foxp3+Treg and Suppresses Type 1 Diabetes in NOD Mice (2013) (33)
- Identification and Validation of Small Molecules That Enhance Recombinant Adeno-associated Virus Transduction following High-Throughput Screens (2016) (33)
- Enhanced Transgene Expression from Recombinant Single-Stranded D-Sequence-Substituted Adeno-Associated Virus Vectors in Human Cell Lines In Vitro and in Murine Hepatocytes In Vivo (2014) (33)
- Insight into the Mechanism of Inhibition of Adeno-Associated Virus by the Mre11/Rad50/Nbs1 Complex (2014) (32)
- Corrigendum: Targeted integration of adeno-associated virus (AAV) into human chromosome 19 (The EMBO Journal (1991) 10 (3941-3950)) (1992) (32)
- scAAVIL-1ra dosing trial in a large animal model and validation of long-term expression with repeat administration for osteoarthritis therapy (2015) (32)
- The genetics of adeno-associated virus. (1984) (32)
- Reducing the Risk of Adeno-Associated Virus (AAV) Vector Mobilization with AAV Type 5 Vectors (2009) (32)
- Safety and biodistribution assessment of sc-rAAV2.5IL-1Ra administered via intra-articular injection in a mono-iodoacetate-induced osteoarthritis rat model (2016) (31)
- Quantitative 3D tracing of gene-delivery viral vectors in human cells and animal tissues. (2012) (31)
- AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo. (2020) (31)
- Adeno associated virus serotype. (2020) (31)
- Analysis of the interaction between adeno-associated virus and heparan sulfate using atomic force microscopy. (2004) (30)
- The Adeno-Associated Virus Genome Packaging Puzzle. (2015) (30)
- Expression of the human glucocerebrosidase and arylsulfatase A genes in murine and patient primary fibroblasts transduced by an adeno-associated virus vector. (1994) (29)
- AAV Recombineering with Single Strand Oligonucleotides (2009) (29)
- Adeno-Associated Virus Vector Mediated Delivery of the HBV Genome Induces Chronic Hepatitis B Virus Infection and Liver Fibrosis in Mice (2015) (29)
- β‐cell‐specific IL‐35 therapy suppresses ongoing autoimmune diabetes in NOD mice (2017) (28)
- Rapid purification of covalently closed circular DNAs of bacterial plasmids and animal tumor viruses. (1980) (28)
- Intermediate filament protein accumulation in motor neurons derived from giant axonal neuropathy iPSCs rescued by restoration of gigaxonin. (2015) (28)
- An Observational Study from Long-Term AAV Re-administration in Two Hemophilia Dogs (2018) (28)
- Protein Phosphatase Inhibitor-1 Gene Therapy in a Swine Model of Nonischemic Heart Failure. (2017) (27)
- Recombinant Adeno-Associated Virus Utilizes Cell-Specific Infectious Entry Mechanisms (2014) (27)
- Recombinant adeno-associated virus: clinical application and development as a gene-therapy vector. (2012) (27)
- Reduced IL‐2 expression in NOD mice leads to a temporal increase in CD62LloFoxP3+CD4+ T cells with limited suppressor activity (2011) (26)
- Efficient expression of protein coding genes from the murine U1 small nuclear RNA promoters. (1996) (25)
- Adeno-associated virus for the treatment of muscle diseases: toward clinical trials. (2010) (24)
- Kinetics of adeno-associated virus serotype 2 (AAV2) and AAV8 capsid antigen presentation in vivo are identical. (2013) (24)
- Intrastromal Gene Therapy Prevents and Reverses Advanced Corneal Clouding in a Canine Model of Mucopolysaccharidosis I. (2020) (24)
- N-acetylaspartate supports the energetic demands of developmental myelination via oligodendroglial aspartoacylase (2016) (24)
- Serotype-specific replicating AAV helper constructs increase recombinant AAV type 2 vector production. (2005) (23)
- AAV-Nrf2 Promotes Protection and Recovery in Animal Models of Oxidative Stress. (2017) (23)
- AAV Biology, Infectivity and Therapeutic Use from Bench to Clinic (2015) (23)
- Identification and Characterization of an Adeno-Associated Virus Integration Site in CV-1 Cells from the African Green Monkey (2003) (22)
- Application of polyploid adeno-associated virus vectors for transduction enhancement and neutralizing antibody evasion. (2017) (21)
- Efficient gene transfer into primary and immortalized human fetal glial cells using adeno-associated virus vectors: establishment of a glial cell line with a functional CD4 receptor. (1997) (21)
- 7 Adeno-associated Viral Vectors (1999) (21)
- Promyelocytic Leukemia Protein Is a Cell-Intrinsic Factor Inhibiting Parvovirus DNA Replication (2013) (21)
- Systemic and Persistent Muscle Gene Expression in Rhesus Monkeys with a Liver De-Targeted Adeno-Associated Virus Vector. (2017) (21)
- Comparison of fetal mesencephalic grafts, AAV-delivered GDNF, and both combined in an MPTP-induced nonhuman primate Parkinson's model. (2013) (20)
- AAV6 K531 serves a dual function in selective receptor and antibody ADK6 recognition. (2018) (20)
- Efficient transduction of vascular smooth muscle cells with a translational AAV2.5 vector: a new perspective for in-stent restenosis gene therapy (2013) (20)
- AAV8 virions hijack serum proteins to increase hepatocyte binding for transduction enhancement. (2018) (20)
- Optimizing gene delivery vectors for the treatment of heart disease (2008) (19)
- NIDDK Workshop on AAV Vectors: Gene Transfer into Quiescent Cells. (1996) (18)
- Transient demyelination increases the efficiency of retrograde AAV transduction. (2010) (18)
- Recombinant adeno-associated virus vectors in the treatment of rare diseases (2015) (18)
- AAV-6 mediated efficient transduction of mouse lower airways. (2011) (18)
- Efficient Capsid Antigen Presentation From Adeno-Associated Virus Empty Virions In Vivo (2018) (18)
- Addressing high dose AAV toxicity – ‘one and done’ or ‘slower and lower’? (2022) (18)
- Expanding the AAV package (2000) (18)
- Preclinical toxicity evaluation of AAV for pain: evidence from human AAV studies and from the pharmacology of analgesic drugs (2014) (17)
- AAV vectors, the future workhorse of human gene therapy. (2003) (17)
- X-linked inhibitor of apoptosis protein-mediated attenuation of apoptosis, using a novel cardiac-enhanced adeno-associated viral vector. (2012) (17)
- Creating a Novel Origin of Replication through Modulating DNA-Protein Interfaces (2010) (17)
- Genetics and Biology of Adeno-Associated Virus (1995) (16)
- The effect of surface demineralization of cortical bone allograft on the properties of recombinant adeno-associated virus coatings. (2008) (16)
- Adeno-Associated Viral Vectors Show Serotype Specific Transduction of Equine Joint Tissue Explants and Cultured Monolayers (2014) (16)
- Site-specific targeting of DNA plasmids to chromosome 19 using AAV cis and trans sequences. (2000) (16)
- Gene therapy for rare diseases: summary of a National Institutes of Health workshop, September 13, 2012. (2013) (15)
- Erratum: Targeted adeno-associated virus vector transduction of nonpermissive cells mediated cells by a bispecific F(ab'γ)2 antibody (Nature Biotechnology (1999)) (1999) (15)
- Minimizing oxidative stress by gene delivery of superoxide dismutase accelerates regeneration after transplantation of reduced‐size livers in the rat (2006) (15)
- Inhibition of antigen presentation during AAV gene therapy using virus peptides (2018) (14)
- Gene Delivery of Activated Factor VII Using Alternative Adeno-Associated Virus Serotype Improves Hemostasis in Hemophiliac Mice with FVIII Inhibitors and Adeno-Associated Virus Neutralizing Antibodies. (2017) (14)
- Delivering multiple gene products in the brain from a single adeno-associated virus vector (2009) (14)
- Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity (2020) (14)
- AAV-mediated gene editing via double-strand break repair. (2014) (14)
- Retinal pigment epithelial cell expression of active Rap 1a by scAAV2 inhibits choroidal neovascularization (2016) (14)
- CLONING OF AAV INTO pBR322: RESCUE OF INTACT VIRUS FROM THE RECOMBINANT PLASMID IN HUMAN CELLS (1982) (13)
- Production of Recombinant Adeno‐Associated Viral Vectors (1999) (13)
- Rapid transgene expression in multiple precursor cell types of adult rat subventricular zone mediated by adeno-associated type 1 vectors. (2012) (13)
- AAV Capsid-Promoter Interactions in the Brain Translate from Rat to the Non-Human Primate. (2020) (12)
- Adeno-associated virus gene therapy vector scAAVIGF-I for transduction of equine articular chondrocytes and RNA-seq analysis. (2016) (11)
- The influence of murine genetic background in AAV transduction of the mouse brain. (2019) (11)
- AAV does the shuffle (2006) (11)
- Methods for adeno-associated virus-mediated gene transfer into muscle. (2001) (11)
- Superior human hepatocyte transduction with Adeno-associated Virus Vector Serotype 7 (2019) (10)
- VHL and PTEN loss coordinate to promote mouse liver vascular lesions (2010) (10)
- Charge-to-Alanine Mutagenesis of the Adeno-Associated Virus Type 2 Rep78/68 Proteins Yields Temperature-Sensitive and Magnesium-Dependent Variants (2000) (10)
- Production of Recombinant Adeno‐Associated Viral Vectors and Use in In Vitro and In Vivo Administration (1999) (9)
- Three-dimensional multipotent progenitor cell aggregates for expansion, osteogenic differentiation and “in vivo” tracing with AAV vector serotype 6 (2012) (9)
- Viral vectors for gene delivery (2015) (9)
- Targeted integration by adeno-associated virus. (2003) (9)
- Optimization of Dexamethasone Administration for Maintaining Global Transduction Efficacy of Adeno-Associated Virus Serotype 9. (2019) (9)
- Heart Failure: A Silver bullet to treat heart failure (2006) (9)
- Impact of neutralizing antibodies against AAV is a key consideration in gene transfer to nonhuman primates (2018) (8)
- In Cellulo Examination of a Beta-Alpha Hybrid Construct of Beta-Hexosaminidase A Subunits, Reported to Interact with the GM2 Activator Protein and Hydrolyze GM2 Ganglioside (2013) (8)
- Methods for the construction and propagation of recombinant adeno-associated virus vectors. (1997) (8)
- Hepatic gene therapy using lentiviral vectors: Has safety been established? (2013) (7)
- Disruption of Microtubules Post-Virus Entry Enhances Adeno-Associated Virus Vector Transduction. (2016) (7)
- AAV Vectors: The Rubik's Cube of Human Gene Therapy. (2022) (7)
- Sub-2 Å Ewald Curvature Corrected Single-Particle Cryo-EM (2018) (7)
- The adeno-associated virus crystal: impact inversely proportional to size. (2002) (6)
- Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates (2013) (6)
- Genetic modification of scAAV‐equine‐BMP‐2 transduced bone‐marrow‐derived mesenchymal stem cells before and after cryopreservation: An “off‐the‐shelf” option for fracture repair (2019) (6)
- Cryoprecipitate augments the global transduction of the adeno‐associated virus serotype 9 after a systemic administration (2018) (6)
- Overcoming Bottlenecks in AAV Manufacturing for Gene Therapy (2018) (6)
- AAV Gene Therapy for Alcoholism: Inhibition of Mitochondrial Aldehyde Dehydrogenase Enzyme Expression in Hepatoma Cells. (2017) (6)
- K137R mutation on adeno-associated viral capsids had minimal effect on enhancing gene delivery in vivo. (2014) (5)
- Adeno-associated virus vectors yield long-term expression and delivery of potentially therapeutic genes into non-dividing neuronal cells (1997) (5)
- [1] Adeno-associated virus: Integrating vectors for human gene therapy (1995) (5)
- Nab Escaping AAV Mutants Isolated from Mouse Muscles. (2018) (5)
- Systemic gene transfer to skeletal muscle using reengineered AAV vectors. (2011) (5)
- Production of Recombinant Adeno‐Associated Viral Vectors and Use for In Vitro and In Vivo Administration (2006) (5)
- Charge-to-Alanine Mutagenesis of the Adeno-Associated Virus Type 2 Rep78/68 Proteins Yields Temperature-Sensitive and Magnesium-Dependent Variants (1999) (5)
- 544. Comparison of AAV Serotype2 Transduction by Various Delivery Routes to the Mouse Eye (2016) (4)
- Chimeric Capsid Proteins Impact Transduction Efficiency of Haploid Adeno-Associated Virus Vectors (2019) (4)
- "D" matters in recombinant AAV DNA packaging. (2021) (4)
- Flies in the ointment: AAV vector preparations and tumor risk. (2021) (4)
- Customized blood-brain barrier shuttle peptide to increase AAV9 vector crossing the BBB and augment transduction in the brain. (2021) (4)
- ADENO-ASSOCIATED VIRUS-BASED VECTORS FOR HUMAN GENE THERAPY (1994) (4)
- Erratum: Corrigendum to "Directed Evolution of a Novel Adeno-associated Virus (AAV) Vector That Crosses the Seizure-compromised Blood-Brain Barrier (BBB)" (Molecular Therapy (2010) 18 (570-578) 10.1038/mt.2009.292) (2010) (4)
- Gene therapy for cardiomyocytes, a heart beat away (2009) (4)
- Employing Factor IX Variants to Avoid Limitations Imposed by Immune Recognition of AAV Vector in Hemophilia B Gene Therapy (2011) (4)
- 19. The Transcapsidation of AAV Serotypes (2004) (4)
- Adeno-Associated Virus Vector Mobilization, Risk Versus Reality (2020) (4)
- Adeno-associated viral vectors for gene therapy (1998) (3)
- Satellite Subgenomic Particles Are Key Regulators of Adeno-Associated Virus Life Cycle (2020) (3)
- Grafts of Dopamine Neurons Can Send Neurites to the Striatum Under GDNF Inducement in a Nonhuman Primate (2009) (3)
- Surface exposed Adeno-associated virus Vp 1-NLS capsid fusion protein rescues infectivity of non-infectious wild-type Vp 2 / Vp 3 and Vp 3-only capsids , but not 5-fold pore mutant virions (2007) (3)
- Insight into the Mechanism of Inhibition of Adeno-Associated Virus by the Mre 11 / Rad 50 / Nbs 1 Complex (2014) (3)
- Bound Protein and Peptide-Based Strategies for Adeno-associated Virus Vector-Mediated Gene Therapy: Where do We Stand Now? (2020) (3)
- Gene Therapy: Introduction and Overview (2007) (3)
- Gene Therapy of CNS Disorders Using Recombinant AAV Vectors (2016) (2)
- 12. Self-Complementary AAV2 Vectors Transduce Liver with the Same Efficiency as AAV8: The Critical Role of Second-Strand Synthesis in AAV Biology (2005) (2)
- Revertant muscle fibers expressing dystrophin do not tolerize the immune system in Duchenne muscular dystrophy: lessons learned from a Phase I clinical trial (96.9) (2010) (2)
- The pros and cons of using the mechanism of AAV site-specific recombination in gene delivery (2003) (2)
- Delivery Systems for Gene Therapy: Adeno‐Associated Virus (2002) (2)
- Vector biophysics: Crystal-clear view (2002) (2)
- Adeno-Associated Viral Vectors for Clinical Gene Therapy in the Brain (2005) (2)
- Adeno-associated viral vectors and successful gene therapy, the gap is closing (2000) (2)
- 493. High Efficiency Gene Targeting to Mammalian Joint Tissue Using Self- Complementary Adeno-Associated Viral Vector Serotypes (2006) (2)
- Department of Health and Human Services, National Institutes of Health, Recombinant DNA Advisory Committee. Minutes of Meeting, December 1-2, 1994 (1995) (2)
- Neurobiology of Disease (2011) (1)
- Recombinant DNA Advisory Committee. Minutes of meeting September 12-13, 1994 (1995) (1)
- Adeno-associated virus 2 co-receptors?-second reply (1999) (1)
- Erratum: Charge-to-alanine mutagenesis of the adeno-associated virus type 2 Rep78/68 proteins yields temperature-sensitive and magnesium-dependent variants (Journal of Virology (1999) 73:11 (9433-9445)) (2000) (1)
- 854. Optimization of AAV Serotype and Promoter for Increased Distribution of Expression in Both Somatic and Central Nervous Systems of Mice (2005) (1)
- Efficiency of gene delivery among AAV serotypes in primate brain (2006) (1)
- 113. Transduction of Neural Cells in Primate Brain Using Adeno-Associated Virus (AAV) Serotypes 2 and 5 (2006) (1)
- Wild type AAV, recombinant AAV, and Adenovirus super infection impact on AAV vector mobilization (2020) (1)
- Corrigendum: Efficient Capsid Antigen Presentation From Adeno-Associated Virus Empty Virions In Vivo (2020) (1)
- Abstract 21651: X-Linked Inhibitor of Apoptosis Protein (XIAP)-Mediated Attenuation of Apoptosis Using a Novel Cardiac Enhanced Adeno-Associated Viral Vector (2010) (1)
- Anti-VEGF Gene Therapy for Wet AMD: Phase I/II Safety and Pharmacology Results (2013) (1)
- Chapter 17:Viral Vectors for Gene Delivery (2010) (1)
- Stimulation of AAV Gene Editing via DSB Repair (2016) (1)
- 14. Next Generation AAV Vectors for Limiting Systemic Leakage and Improving Safety Following CNS Administration (2015) (1)
- recombinant AAV vectors in human cell lines in vitro and in murine hepatocytes in (2014) (1)
- From crystal structure to clinic: highlights of the Tenth International Parvovirus Workshop. (2005) (1)
- development of hemophilic synovitis in the absence of circulating factor IX Intra-articular factor IX protein or gene replacement protects against (2013) (1)
- Cellular and structural characterisation of VP1 and VP2 knockout mutants of AAV3B serotype and implications for AAV manufacturing. (2022) (1)
- Viric vectors and their preparation and administration procedures. (1999) (0)
- 11. Reporter Gene-Based Analysis of rAAV Genome Circularization and Recombination (2004) (0)
- P17 24 MP – INITIAL CHARACTERIZATION OF RADIATION-INDUCED SOLID TUMORS IN A TRANSGENIC MOUSE LINE (1991) (0)
- CV-1 Cells from the African Green Monkey Adeno-Associated Virus Integration Site in Identification and Characterization of an (2002) (0)
- 94. Targeting Endothelial Cells in Mice with Adeno-Associated Virus Serotype 1 Vector (2004) (0)
- Self-Complementary Adeno-Associated Viruses (scAAV) Transduce Anterior Segment Tissues of Living Rats and Monkeys Without Detrimental Secondary Effects (2007) (0)
- AAV-Mediated Nrf2 Gene Replacement in the Nrf2 Knockout Mouse (2012) (0)
- Viral vectors for CNS disorders (2015) (0)
- Mavis Agbandje-McKenna's lifelong commitment to teaching and research. (2021) (0)
- Novel Approaches for Production of Recombinant Adeno-Associated Virus (2006) (0)
- AAV Vector Transduction Restriction and Attenuated Toxicity in hESCs via a Rationally Designed Inverted Terminal Repeat (2022) (0)
- Corrigendum: Gene therapy approaches for equine osteoarthritis (2023) (0)
- U . S . Patent May 19 , 1998 Sheet 2 of 5 5 , 753 , 500 AAV PROBE 2 3 4 5 6 7 8 9 O 2 3 D C C (2017) (0)
- United States Patent Samulski (2017) (0)
- AAV vector mobilization, risk vs reality. (2020) (0)
- AAV Gene Therapy in a Canine Model of MPS1 Prevents and Reverses Corneal Blindness (2017) (0)
- Anti-VEGF Gene Therapy for Wet AMD: Safety and Tolerability of Subretinal Delivery in a Phase I/II Clinical Trial (2013) (0)
- 739. Bioluminescent Virion Shells: A Novel Tool for Visualization of Viral Vectors in Animal Tissue (2006) (0)
- Direct comparison of epifluorescence and immunostaining for assessing viral mediated gene expression in the primate brain (2022) (0)
- Neutralizing Antibody Dynamics in scAAV Dosed Horses (2012) (0)
- Virus vectors and methods for their manufacture and administration. (1999) (0)
- 7. Adeno-Associated Virus Type 2 (AAV2) Contains an Integrin alpha5beta1 Recognition Sequence Essential for Viral Cell Entry (2006) (0)
- Abstract 2882: Directed Evolution of Cardiac Specific Adeno-Associated Vector Variants (2008) (0)
- Adeno-associated virus vectors for human gene therapy (2020) (0)
- Genes of Factor VIII and Factor IX and modified vectors for gene therapy (2007) (0)
- Breakthroughs and barriers in clinical gene therapy (2015) (0)
- Trafficking of an Adeno-Associated Virus Variant in the Retina (2012) (0)
- WILD-TYPE ADENO-ASSOCIATED VIRUS DISCOVERY TO VECTORIZATION Adeno-associated virus discovery (2015) (0)
- 238. A Comparison of Gene Delivery and Vector Systems to Achieve High Levels of Sustained Skeletal Muscle Gene Expression (2004) (0)
- Methods to increase the effectiveness of the product of recombinant AAV. (1998) (0)
- Development of AAV vectors for the therapy of autoimmune and inflammatory diseases (2010) (0)
- Impact of neutralizing antibodies against AAV is a key consideration in gene transfer to nonhuman primates (2018) (0)
- ADENO-ASSOCIATED VIRUS (AAV) CAN BE USED AS A POTENTIAL VECTOR TO TRANSFER GENES INTO PANCREATIC ISLETS (1992) (0)
- Curing ultra-rare diseases while ensuring access, equity and affordability (2020) (0)
- , Impact on Cellular Gene Expression Empty Adenovirus Capsids and Their Development and Characterization of Novel (2003) (0)
- Compositions and methods for improved parvovirus transduction (2011) (0)
- 104. Role of the HI Loop in the Adeno- Associated Virus (AAV) Life Cycle (2006) (0)
- Sub-2 Å Ewald curvature corrected structure of an AAV2 capsid variant (2018) (0)
- 18. Facilitation of AAV Genome Circularization by Host Cell Factors Involved in DNA Replication and Double-Strand Break Repair (2005) (0)
- The transduction of myoblasts by means of adeno-associated virus vectors (1996) (0)
- Proteasome Inhibitors by of Adeno-Associated Virus Transduction Mechanistic Insights into the Enhancement (2014) (0)
- Methods and compounds for controlling the release of parvovirus vectors reconbinantes. (2001) (0)
- Adeno-associated virus vectors; Gene therapy and viral vectors, the gap is closing (1999) (0)
- 343. Repair of Thalassemic |[beta]|-Globin pre-mRNA by Antisense AAV and Lentiviral Vectors in Cell Culture (2005) (0)
- A New, Non–Imunogenic Gene Therapy Vector for the Human Trabecular Meshwork: scAAV (self–complementary Adeno–Associated Virus) (2005) (0)
- Elucidating the mechanism behind enhanced retinal transduction of an AAV2 variant (2013) (0)
- Recombinant Adeno-Associated Virus Production, the Beginning of the End of Uncertainty. (2022) (0)
- Mavis Agbandje-McKenna's Lifelong Commitment to Teaching and Research. (2021) (0)
- Adeno-Associated Virus Type 2 Contains an Integrin (cid:2) 5 (cid:3) 1 Binding Domain Essential for Viral Cell Entry (2006) (0)
- 464. Development of a Novel Gene Regulation System Downstream of Promoter (2005) (0)
- Gene Therapy: Technology (2006) (0)
- The Growing Promise of Gene Therapy Approaches (2018) (0)
- Intravitreal AAV-mediated expression of Nrf2 promotes retinal recovery from light-induced retinopathy in mice (2015) (0)
- Inducible Transgene Expression After Intraocular Injection of an Inducible Expression Cassette Packaged in Adeno-Associated Viral (AAV) Vector (2008) (0)
- Recombinant adeno-associated virus: clinical application and development as a (2012) (0)
- 959. Pharmacokinetic Studies of Human IFN-|[szlig]| in Mice Following Gene-Based Delivery (2005) (0)
- Generation of a Mouse Model for Studying AAV Targeted Integration (1999) (0)
- 403. Defined Vector Substrates Used To Probe rAAV DNA Integration (2005) (0)
- AAV-mediated activation of the Nrf2 pathway in the Nrf2-deficient mouse (2014) (0)
- Hemophilia B Mouse Lines Doubly Humanized for Human F9 and MHC Class II Genes Advance Specificity of Inhibitor Study (2011) (0)
- Serotype-specific transduction of canine joint tissue explants and cultured monolayers by self-complementary adeno-associated viral vectors (2022) (0)
- Methods for manufacturing microstructures and nanostructures using soft lithography or printing (2004) (0)
- Structure and dynamics of Adeno-Associated Virus 1 serotype 1 VP 1-unique N-terminal domain and its role in 2 capsid trafficking (2013) (0)
- Colocalization ofAdeno-Associated VirusRepandCapsidProteins intheNuclei ofInfected Cells (1992) (0)
- Abstract 714: Direct Comparison of AAV Serotypes 1 9; Onset of Gene Expression, Time to Peak Expression, and Fate of Viral Genomes in Mice after Skeletal Muscle, and Tail Vein Injection (2006) (0)
- Methods for the preparation of isolated micro- and nano-structures using soft lithography or printing lithography (2004) (0)
- 93. Development of AAVidua Vector for the Treatment of Cornea Associated Vision Loss in Bone Marrow Treated-Hurler Patients (2016) (0)
- AAV Gene Therapy for MPS1 Corneal Clouding and Joint Stiffness (2015) (0)
- REVIEW Bound Protein- and Peptide-Based Strategies for Adeno-Associated Virus Vector-Mediated Gene Therapy: Where Do We Stand Now? (2020) (0)
- Jean-Michel Vos (2001) (0)
- Are Facilitated by Microtubule Network Adeno-Associated Virus Type 2 Particles Escape , and Perinuclear Accumulation of Cytoplasmic Trafficking , Endosomal (2012) (0)
- AAV Gene Therapy for MPS1 Corneal Clouding (2015) (0)
- Efficient expression of protein coding genes from the murine Ul small nuclear RNA promoters (vectors/adenovirus/gene therapy) (1996) (0)
- 91. Universal purification of AAV serotypes 1|[ndash]|5 modified to contain a heparin binding epitope (2004) (0)
- Royal academy of medicine in Ireland section of ophthalmology (1995) (0)
- Self-complementarity in adeno-associated virus enhances transduction and gene expression in mouse cochlear tissues (2020) (0)
- 251. Defining Conserved Structural Components of the AAV Capsid That Enable Tissue-Specific Transduction Following Systemic Administration (2016) (0)
- " Verdohemochrome IXa : Preparation and oxidoreductive cleavage to biliverdin IXa (2003) (0)
- Diabetes IL-2 Gene Therapy Prevents Autoimmune Inducible Adeno-Associated Virus-Mediated (2011) (0)
- AAV-mediated treatment of retinal degeneration in the Nrf2 knockout mouse (2013) (0)
- Transduction of Mouse Retina by Intravitreal Delivery Using Chimeric Capsids with Altered Glycan Interactions (2015) (0)
- Adeno-associated virus vectors for gene transfer into erythroid cells. (1996) (0)
- Gene therapy approaches for equine osteoarthritis (2022) (0)
- 17. Role of Vp2 in AAV Packaging (2004) (0)
- Genetically Expressed Monodisperse α Helical Polypeptides (1996) (0)
- Corrigendum to "Directed Evolution of a Novel Adeno-associated Virus (AAV) Vector That Crosses the Seizure-compromised Blood-Brain Barrier (BBB)". (2010) (0)
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